3rd c4c Multistakesholder Meeting
A 3rd c4c Multistakeholder Meeting (MSM) was held on 21 February in Berlin; the topic was medical devices for children with Type 1 diabetes.
Patients, Families & the Science of Rare Diseases
On the 28th February, we commemorated Rare Disease day. The majority of rare diseases affect children, with an estimated 70% having a Paediatric onset (source www.eurordis.org). There is a huge, unmet need to develop effective drugs for children with rare diseases. Currently, only 5% of rare diseases have an effective treatment option.